• A smiling teenage boy wearing a plaid shirt. In the background, a pattern of genetic code. Caption is Elijah, living with limb-girdle muscular dystrophy.
    ELIJAH Living with Limb-girdle
    muscular dystrophy
    ELIJAH Living with LGMD

    Welcome to SareptAcademy A COMMUNITY RESOURCE CENTER

    At Sarepta, we are committed to a patients-come-first approach. We are working directly with people living with rare genetic conditions, and with parents and care partners who are living with, or caring for, someone with a rare genetic condition.

    Our goal is to make useful, easy-to-understand information available to everyone. SareptAcademy is a space where you may learn about:

    • the science behind these complex conditions
    • the strategies doctors are using to treat people living with rare conditions
    • how drugs are developed
The resources on this site can help you feel more confident and make more informed decisions.
ICON: DNA helix A Focus on Rare
Conditions
ICON: Microscope Understanding
Our Science
ICON: Medicine vial and syringe How Drugs Are
Developed

Two rare conditions are our company’s priority today

Sarepta is dedicated to finding therapies for complex, rare, genetic disorders.

Duchenne Muscular Dystrophy (DMD)

Learn about the most common form of childhood muscular dystrophy

Limb-Girdle Muscular Dystrophies (LGMDs)

Learn why genetic testing is especially important for this family of rare conditions